NMDP BioTherapies and Cryoport collaborate to Accelerate the Development of Cell and Gene Therapies
NMDP BioTherapies, an organization offering solutions for companies developing and commercializing cell and gene therapies, and Cryoport (NASDAQ: CYRX), a leading global provider of innovative [...]
Two Gene Therapy Products for Sickle Cell Anemia Approval by FDA
Two gene therapy products, Casgevy and Lyfgenia, have been approved by the FDA for the treatment of patients 12 years and older with sickle cell anemia. The FDA approved Casgevy to Vertex [...]
Lipid Nanoparticles for Muscle-selective mRNA Delivery
Researchers based at the University of Toronto Leslie Dan Faculty of Pharmacy have developed a novel ionizable lipid nanoparticle (LNP), called iso-A11B5C1, that can deliver mRNA specifically to [...]
Most of Today’s Gene Therapies Rely on Viruses — and that’s a Problem
Around the world, more than 2,000 gene therapies are in development, according to the American Society of Gene and Cell Therapy, which are financially attractive to drug companies. It seems the [...]
